Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.
As noted recently in an article published by Cancer Network, the FDA has cleared CYNK-001 for use in COVID-19 patients. When the investigational new drug (IND) application is submitted to…
Continue ReadingCYNK-001 Application Cleared by the FDA for use in COVID-19 Patients
According to an article in the Asco Post, the FDA granted accelerated approval to Merck's KEYTRUDA®, pembrolizumab, for the treatment of metastatic small cell lung cancer (SCLC). The drug targets…
Continue ReadingFDA Approves Merck’s KEYTRUDA® in Small Cell Lung Cancer
According to a recent article in the Harvard Gazette, researchers from Harvard announced the results of a study involving animal models that brought about immunity and lasting recovery against acute…
Continue ReadingHarvard Study Presents an Injectable Vaccine Causing Immunity Against Acute Myeloid Leukemia (AML) in Mice
Seattle Genetics, Bothell, Washington recently issued an announcement through Drugs.com that the FDA approved Tukysa™ combined with capecitabine and trastuzumab for patients with metastatic HER2-positive breast cancer. The drug combination…
Continue ReadingThe FDA Approves Tukysa™ for Metastatic HER2-Positive Breast Cancer
Seneca Biopharma, Germantown, Md., issued a press release announcing its recent meeting with the FDA to discuss elements of a final design and protocol for a Phase 3 trial investigating…
Continue ReadingSeneca Biopharma Preparing for its Phase 3 Trial to Test NSI-566 for Amyotrophic Lateral Sclerosis
According to a report by ABC News, Virtua Health, one of the largest healthcare providers in New Jersey, claimed to have a forty-year history of organ transplant completions. Nonetheless, a…
Continue ReadingHe Waited Five Years to Receive a Kidney Transplant and Then the Kidney Was Given to the Wrong Patient
According to an article in Science Daily, Professor David Nicewicz and a team of researchers at the UNC Department of Chemistry, discovered a method of creating tracers used in…
Continue ReadingResearchers Use Positron Emission Tomography (PET) to Track Drugs and Image Medical Conditions
During the past fifteen years there has been ever-increasing interest in scientific research in the role of microbiome in human health. According to a recent article in Forbes India, this…
Continue ReadingGut Bacteria May Soon be Treating a Wide Range of Illnesses
A two-part series of “The Gene”, a PBS documentary, will air on April 14, 2020. The film, by Ken Burns, is based on a book with the same title written…
Continue ReadingGenetic Engineering: PBS Documentary “The Gene” to Air April 14, 2020
According to a recent article in Parkinson’s News Today, the drug prasinezumab has entered the second half of a Phase 2 trial. An earlier trial, NCT02157714, showed that the therapy…
Continue ReadingResearchers are Testing a Drug That May Slow the Progression of Parkinson’s Disease
Results of one of the largest and most important studies in a decade, the International Study of Comparative Health Effectiveness with Medical and Invasive Approaches (ISCHEMIA), were just announced.…
Continue ReadingHeart Disease: Cardiologists Have Been Debating for Decades and the Results Are In
The drug levodopa and most other therapies developed over the years for Parkinson's disease have been centered on correcting the lack of dopamine. Researchers acknowledge that the reason dopamine…
Continue ReadingParkinson’s Disease: A New Study Focusing on Preventing the Loss of Dopamine Producing Neurons
Michael and Armené Kapamajian were at home in Los Angeles settling in with their one week old baby, Sasoun, when their doctor called and asked them to come in…
Continue ReadingSevere Combined Immunodeficiency: After Quarantine With Their Baby, This Family Was Prepared for Coronavirus
Dr. Pierre Fenaux, of Hôpital Saint Louis, Paris and lead author of the MEDALIST trial, told Ash Clinical News that treatment with the investigational drug, luspatercept, improved the rate of…
Continue ReadingMEDALIST Trial: The Need for Blood Transfusions Was Reduced in Myelodysplastic Syndrome Patients
Researchers find stents, surgery provide higher quality of life for those with chest pain. Invasive procedures such as bypass surgery and stenting—commonly used to treat blocked arteries—are no better at…
Continue ReadingNIH-funded studies show stents and surgery no better than medication, lifestyle changes at reducing cardiac events
In February 2020, Epigenetics published results of a study reporting that researchers have found an early sign of Alzheimer’s disease in DNA modification (methylation) that had been overlooked. Patients…
Continue ReadingResearchers Have Found an Early Sign of Alzheimer’s Disease in DNA Modification
In a Special Issue of the journal Disease Models and Mechanisms Highlights, James J. Dowling et al describes pediatric neuromuscular diseases as mostly genetic and affecting areas of the peripheral…
Continue ReadingThis Journal Highlights Current Research on Neuromuscular Diseases (NMD)
Pam Kelley, a reporter whose focus is on the challenges facing people below the poverty level, submitted this story to the Charlotte Magazine. Pam conducted interviews with Cheryl Potts over…
Continue ReadingIs Poverty a Rare Disease? A Woman in North Carolina with Sarcoidosis Shares Her Struggle
A recent article published in India’s Pharma Literati cites The World Health Organization as not having endorsed a definition for rare diseases. The European Union defines 'rare' as less than…
Continue ReadingReview of Rare Movement Disorders in India and the United States
According to a recent article published in Pharmaceutical-Technology, uniQure’s gene therapy AMT-130 may lower levels of the huntingtin protein that causes the disorder. An abnormal gene is responsible for damage…
Continue ReadingWill Gene Therapy Finally Provide a Cure for Huntington’s Disease?
A recent Biospace article covers a news release from 4D Pharma in Leeds, England. 4D has announced the first worldwide clinical confirmation of a biotherapeutic product. MRx0518 has been combined…
Continue ReadingBiotherapeutics Reduced This Patient’s Tumors After Seven Other Therapies Failed
TARGET PharmaSolutions Inc. recently announced enrollment of the first patients in its ten year, ten thousand patient asthma study. Professor Michael Wechsler, M.D. pulmonologist at the National Jewish Health organization…
Continue ReadingTen Year TARGET-ASTHMA Study Using Data for New Therapies and to Develop New Drugs
Biological engineers at MIT are using a new technique to study various organs and their interaction with our immune system. According to a recent article in Science Daily, the researchers…
Continue ReadingOrgans-On- A-Chip: A Novel Approach to Studying Inflammatory Bowel Disease
Identifying biomarkers may be an improved method of classifying Alzheimer’s and Parkinson’s. As outlined in a recent article covered by Parkinson's News Today, both diseases are diagnosed for the most…
Continue ReadingUsing Artificial Intelligence to Study Alzheimer’s and Parkinson’s Disease
859 words vs 970 words 8% An article recently published in Science Daily quotes the results of a study showing a favorable outcome for six out of nine x-linked chronic…
Continue ReadingA Favorable Outcome for CGD Patients Post Stem Cell Gene Therapy
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Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.