Chemotherapy-induced peripheral neuropathy, or CIPN, is a common side effect of chemotherapy. A recent study aimed to uncover whether or not oxaliplatin chemotherapy increased risk of CIPN for those with…
By Caitlin Seida from In The Cloud Copy CRISPR-Cas9, often called just CRISPR, is a technique used to quickly edit DNA to alter gene functions. Think of it like the…
Janssen Pharmaceuticals has an ongoing Phase 1/2 clinical trial for the inherited retinal disease X-linked retinitis pigmentosa (XLRP). They are investigating an adeno-associated gene therapy called RPGR as a therapeutic…
Scares That Care Scares That Care is a 501(c)(3) organization, first established in 2007 by Joe Ripple, dedicated to fighting the "monsters" of childhood illnesses, breast cancer, and burns. They support…
The EveryLife Foundation has initiated a scholarship fund to help those with rare conditions pursue their academic dreams. These will be one-time awards of 5,000 dollars. Up to 32 patients will…
Biopharmaceutical company Theratechnologies Inc. recently announced that its therapy candidate tesamorelin is effective in the treatment of HIV-associated nonalcoholic steatohepatitis (NASH). According to new data, published in JCI Insight, tesamorelin…
In a recent webinar hosted by the International Waldenström's Macroglobulinemia Foundation (IWMF) and held on July 22nd, 2020, Dr. Jeffery Matous from the Colorado Blood Cancer Institute gave an in-depth…
BioMarin has recently submitted a Marketing Authorization Application to the European Medicines Agency for their achondroplasia treatment, vosoritide. As of now, the review of the application will begin in August.…
There's no misunderstanding this fact: renal-replacement therapy is effective for patients with severe acute kidney injuries (AKI). However, states Kenny Walter in MD Magazine, the efficacy of this treatment can depend…
According to a story from Charcot-Marie-Tooth News, a new nonprofit organization called Shark Tooth Cycling has recently begun operations. The mission of the organization is to encourage young people in…
Thanks to the rampant spread of COVID-19, many events, symposiums, and clinics moved online. One was the 2020 ACR State-of-the-Art Clinical Symposium, in which participants discuss diagnostic information, treatments,…
During EHA25 Virtual, researchers presented on hematological concepts and the future of diagnosis, treatment, and research. One such presentation discussed results from the InHIBIT-Bleed study, which examined the efficacy…
Thanks to COVID-19, many annual meetings and other events have been held online this year. One such event was the American Society of Retina Specialists (ASRS) Virtual Annual Meeting,…
When Emilia Galarneau grows up, she'll have quite an exciting story to tell about her birth. According to the Connecticut Children's Medical Center, Emilia was born on March 6th,…
In a new article in the journal Science Advances, neuroscientists have found a specific mechanism that is responsible for the familial migraines. A type of brain cell called astrocytes have…
The Michael J. Fox Foundation has awarded a grant of $750,000 to researchers at the University of California, Los Angeles for their work to improve the Parkinson's disease registry in…
It's no secret that stress, anxiety, and depression can negatively affect us physically. But according to Myasthenia Gravis News, researchers also linked stress and depression to increased relapses for…
According to a story from Medscape, the US Food and Drug Administration (FDA) has recently approved a new oral solution as a treatment for symptoms associated with narcolepsy, a rare…
July 30th, 2020 is recognized as Gastroschisis Awareness Day. This event aims to help spread awareness about gastroschisis, a rare birth defect, among both the general public and within the…
When the team at Freiburg University discovered the domain of the T-cell receptor they were surprised that the newly-coined “RK motif” had never been identified. According to a recent…
As society progresses, certain diseases or conditions become more and more prevalent. For example, chronic conditions like osteoporosis or diabetes have rapidly risen over the past decade. Now, according…
According to a story from Globe Newswire, the biopharmaceutical company Ovid Therapeutics and the University of Connecticut School of Medicine (UConn) have announced a new license agreement and research collaboration…
According to a story from The Island Packet, fourteen year old Presley Miller, of Hilton Head Island, SC, was recently confirmed to have died from complications related to the rare…
Happy Friday! July is almost over, which means that Juvenile Idiopathic Arthritis Awareness Month is drawing to a close. But it's not too late to bring attention to this often…
According to a story from The Philadelphia Inquirer, 25 year old Gabby McNary isn't taking any risks when it comes to the coronavirus/COVID-19 pandemic. Philadelphia was hit hard by the…
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