A recent article in the Korea Biomed Review reported that the joint research effort by Seoul National Medical College and Helixmith of San Diego, California, found Helixmith’s VM507 antibody effective…
When Jacqueline City went to a concert in high school, she didn't know that her life was about to change forever. At the time, Jacqueline was 18 and living in…
For years, scientists believed there might be a connection between amyotrophic lateral sclerosis and frontotemporal lobar degeneration (FTLD), also sometimes known as frontotemporal dementia. However, researchers from Osaka University may…
As reported in Newswise; this week, researchers across the world have been given access to a new guide that could fundamentally better the outcomes of people living with chronic kidney…
Recently, IVX Health announced the opening of three new Tampa-based infusion centers to treat patients with chronic conditions. Currently, IVX Health, who describes themselves as "[providing] biologic injections and infusions…
New Zealand has the third highest rate of inflammatory bowel disease (IBD) in the world, but there are only two drugs that are currently being funded to treat it. As…
According to a story from The Garstang Courier, Joshua Brandwood of Lancaster, UK has begun organizing a 5K run as a fundraiser for the family of Lexi Tindale, a girl…
For patients with rare diseases and their families, life is sometimes isolating. It can be difficult to explain your condition. At the same time, it is incredibly important to find…
According to a story from Charcot-Marie-Tooth News, a recent study suggests that the three components of the investigational therapy PXT3003 work in synergy to improve the condition of patients with…
Have you ever heard of the Neupro patch? This transdermal delivery system directly delivers a dopamine agonist called rotigotine into the body. For patients with Parkinson's disease, restless legs syndrome,…
As reported in Stem Cells News; finding the right donor for people in need of bone marrow transplants can be very tricky. This is because finding the correct match between…
Claire Brinkley Claire Brinkley's daughter Eleanor is diagnosed with progressive familial intrahepatic cholestasis (PFIC) which is a rare disease affecting the liver. As a newborn, she appeared perfectly normal. But at…
There are over 24 million diagnosed cases of COVID-19 worldwide, with over 800,000 associated deaths. The viral pandemic certainly has people feeling upset, confused, and vulnerable. Unfortunately, some resources are…
Earlier this week, Sarepta Therapeutics announced that the FDA approved a New Drug Application (NDA) for Casimersen (SRP-4045). The treatment, for patients with exon 45 amenable Duchenne muscular dystrophy (DMD),…
According to Charcot-Marie-Tooth News, biotechnology company Helixmith recently began a Phase 1/2a clinical trial to test the efficacy of Engensis (VM202) for patients with Charcot-Marie-Tooth disease type 1A (CMT1A). The…
What do microcephaly, Zika virus, Dengue fever, and COVID-19 have in common? According to a recent press release, HP163 could be a treatment for all four. Developed by biopharmaceutical company…
According to a story from BioSpace, the biotechnology company Tiziana Life Sciences plc has announced that it was recently granted a patent from the United States Patent and Trademark Office…
CohBar has initiated dosing in their Phase 1b trial of CB4211, which is a treatment for nonalcoholic steatohepatitis (NASH). The biotechnology company focuses on mitochondria based therapies with the goal…
Professor Illana Gozes and her team at Tel Aviv University recently developed NAP (CP201). It is an experimental drug that has been proven to be effective in the treatment of…
The importance of potassium restrictions in the diets of chronic kidney disease (CKD) patients has been stressed for years. It lowers levels of serum potassium, therefore lowering the mortality risk.…
According to a story from Charcot-Marie-Tooth News, the nonprofit organization CMT Australia, which focuses on serving the Charcot-Marie-Tooth disease patient community in Australia, has recently acquired a grant to the…
According to a story from BioSpace, the biopharmaceutical company Cerecor Inc., has recently announced that it has restarted operations of its phase 1b clinical trial. This trial is evaluating the…
The Michael J. Foxx Foundation (MJFF) has recently award $8.8 million of grants to various medical professionals for their research on Parkinson's disease. The aim is to develop more treatments,…
According to a story from hemophilia.org, the drug company Ferring Pharmaceuticals issued a recall of the nasal spray drug desmopressin (marketed as Stimate) on July 21st, 2020. This product is…
The biotechnology company ContraFect has entered into an agreement with the Cystic Fibrosis Foundation. This funding agreement aims to investigate and develop direct lytic agents (DLAs) as a treatment for…
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