According to a recent story from pm360online.com, the pharmaceutical company Shire announced that the marketing application for its drug product lanadelumab has gained approval from the European Medicines Agency (EMA).…
According to a recent story from CityNews Toronto, Alara Ozkose's Dravet syndrome was preventing her from being able to live a life that was even close to normal. She was…
According to a story from Newswise, researchers at the University of Texas Southwestern Medical Center are reporting the a new drug developed for the treatment of rare, pediatric cancers, has…
According to a story from the Seattle Times, a massive $150 million gift from Richard and Susan Rogel to the University of Michigan is slated to go towards the school's…
According to a story from mrknewsroom.com, the pharmaceutical companies Merck and AstraZeneca recently announced that the marketing application for the investigational drug olaparib (brand name Lynparza) was recently certified for…
According to a story from the Independent, father Nick Sireau is worried that Brexit, the United Kingdom's plan to withdraw from the European Union, could affect the ability of his…
According to an announcement from the pharmaceutical company Retrophin, Inc., the company is starting to move forward with phase 3 trials for its drug candidate sparsentan. The drug is in…
According to a story from biopharmadive.com, the pharmaceutical company Roche is reporting a total of five deaths of patients with hemophilia A that have taken the company's product Hemlibra. While…
According to a story from 4-traders.com, the pharmaceutical company SteroTherapeutics recently announced that its drug candidate ST-002 was awarded Orphan Drug Designation by the U.S. Food and Drug Administration (FDA).…
According to a story from rte.ie, a team of scientists from the Trinity College Dublin have managed to discover a new technique that allowed them to shut down inflammatory response…
According to a story from the Sunderland Echo, a man from the Sunderland area, Graydon Downs, was diagnosed with glioblastoma when he was just 33 years old. At that time,…
According to a story from sunmag.net, 23andMe, the genetics testing company widely known for its ancestral analysis measures, is now offering a genetics test to measure your risk of BRCA1…
According to a story from Chronicle Live, a medical team from Newcastle in the UK will travel to the Kerala province in southern India to treat patients with hemophilia. The…
According to an article from VCU Massey Center's blog, a team of researchers from the VCU Massey Cancer Center have successfully discovered a pair of genes that could be essential for…
A story from Charcot-Marie-Tooth News highlights the necessity for genetic testing and a physical examination prior to chemotherapy in order to prevent nerve damage in people with asymptomatic Charcot-Marie-Tooth disease…
According to a story from SMA News Today, a recent study has demonstrated that the parents of children with spinal muscular atrophy are often skeptical about enrolling their kids in…
According to a story from Wave Newspapers, Danielle Guinn, a woman diagnosed with cerebral palsy and epilepsy, is not letting her disability slow her down, and is currently participating in…
According to a story from asianscientist.com, a group of Japanese researchers have managed to unearth a genetic mutation that is associated with progressive supranuclear palsy. The discovery is helping scientists…
According to a story from watoday.com.au, Reginald Whiu, aged 73, had been complaining about back pain and was diagnosed with degeneration of the spine by his doctor. This was at…
According to an article from Righting Injustice, a recent study suggests that TNF inhibitors may increase the risk of rare cancers in pediatric patients. The study recommends that children that…
An article from SRN News is reporting that a lot of people with familial hypercholesterolemia are going through life without getting the treatments that could help them, such as statins.…
According to a story from triblive.com, Roger Ziegler has self-published a book about his family's experience with his son Noah. Noah is now a healthy 24-year-old, but there were multiple…
According to a story from the Lancashire Telegraph, Dr. John Timms, age 48, was recently diagnosed with a rare and deadly form of cancer: mesothelioma. Dr. Timms had committed much…
According to a story from biopharmadive.com, the Swiss pharmaceutical company Novartis has entered a partnership with researchers from the engineering and applied sciences school at Harvard University. The team will…
According to a story from curetoday.com, a recent study indicated that many patients with uveal melanoma reported having unmet psychological and informational needs, particularly in the first several months after…
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