Biohaven Pharmaceutical Holding Company Ltd. announced at the end of last month that the company has completed enrollment in its Phase 3 clinical trial of trigriluzole in spinocerebellar ataxia (SCA)…
In April of this year, Argos Therapeutics reported interim results from its Phase 3 ADAPT clinical trial of rocapuldencel-T in combination with the normal standard-of-care for the treatment of newly…
The week before last, innovative biopharmaceutical company DelMar, presented data at the Pediatric Neuro-Oncology Basic and Translational Research Conference from a clinical research with VAL-083 in chemo-resistant glioblastoma patients. Glioblastoma is…
The biopharmaceutical research and development company CytRx Corporation, announced an exciting new update early this month involving the company’s work with aldoxorubicin, a new drug for treatment in soft tissue sarcomas.…
Cystic Fibrosis… For a mother, those words are disheartening, confusing, and so, so frightening. For a child, those words mean countless daily medications, extensive hospital visits, and a shortened life…
Albireo Pharma is in the midst of preparing for an exciting Phase 3 clinical trial to test A4250 for the treatment of progressive familial intrahepatic cholestasis (PFIC). PFIC is a…
Onxeo has recently received the 10th unanimous recommendation from the Data Safety Monitoring Board to continue with the Phase 3 study (coined ReLive) of Livatag®. Livatag® is designed for use…
Xynomic Pharma, a United States-based oncology research and development company, announced at the end of last month that it had entered into a partnership with the University of California San…
The Danish biotechnology company, Orphazyme, announced in early May of this year that enrollment was completed for its lead study program for Niemann-Pick type C disease. Niemann-Pick disease is a…
Support for Ofev® just keeps coming! Ofev® (nintedanib) was first approved by the U.S. FDA in 2014 for the treatment of idiopathic pulmonary fibrosis (IPF) after clinical trials, especially the INPULSIS…
Results from the Phase 3 CASTOR trial from Janssen Pharmaceutical Companies were recently released, finding that Darzalex (daratumumab) was extremely effective at reducing the risk of multiple myeloma progression or…
GW Pharmaceuticals sta scoprendo ... Epidiolex® (fabbricato e testato da GW Pharmaceuticals) è un candidato medico cannabinoide medico per il trattamento di sindromi di epilessia rara, resistente e precoce, come…
GW Pharmaceuticals découvre ... Epidiolex® (fabriqué et testé par GW Pharmaceuticals) est un candidat cannabinoïde médical leader pour le traitement de syndromes d'épilepsie rares, résistants et débutants tels que le…
De grandes nouvelles pour les patients atteints d'un cancer du sein métastatique muté par le BRCA: un traitement connu contre le cancer de l'ovaire a passé des essais cliniques de…
Aerie Pharmaceuticals announced exciting efficacy results from the second part of its Phase 3 clinical trial of Roclatan at the end of last month. Roclatan is devised for a group…
Notizie grandi per i pazienti con tumore metastatico mutato BRCA mutato: un trattamento con cancro ovarico conosciuto ha superato le sperimentazioni cliniche di fase III per il tumore metastatico mutato…
Alexander Davis è di Tipton, Indiana. Ha vissuto con atrofia muscolare spinale (SMA). SMA lo impedisce di muoversi molto e non è in grado di camminare. Pertanto, ha bisogno di…
Alexander Davis est originaire de Tipton, Indiana. Il a vécu avec une atrophie musculaire spinale (SMA). SMA l'empêche de bouger beaucoup et il est incapable de marcher. Par conséquent, il…
Notizie emozionanti per le persone che vivono con sarcoidosi! Vanderbilt University Medical Center (VUMC) ha sviluppato un Centro Sarcoidosi di Eccellenza. Attualmente, il dottor Wonder Drake è il direttore del…
Want some more news, events and announcements on hemophilia? We got 'em! [one_half] [/one_half] [one_half_last] FDA Clears New Drug for Hemophilia B Treatment Virtual-reality Game Helps This Boy…
Fino a poco tempo fa, il termine ROHHAD non significava nulla. Ma poi ho sentito parlare di un bambino canadese di 11 anni chiamato Denika Bailey che ha questo raro…
L'emiplegia si verifica normalmente durante la gravidanza, o molto rapidamente dopo la nascita. I genitori sono fortunati ad avere alcuni momenti con il loro bambino prima che questa condizione cambia…
L'hémiplégie se produit normalement pendant la grossesse, ou très rapidement après la naissance. Les parents ont de la chance d'avoir quelques instants avec leur enfant avant que cette condition ne…
Je suis sûr que vous avez entendu parler de la SLA après que le «Défi du dégel de glace» ait balayé la nation en 2014, mais peu ont probablement pris…
Sono sicuro che hai sentito parlare di ALS dopo che la "Ice Bucket Challenge" ha spazzato la nazione nel 2014, ma pochi ancora probabilmente hanno preso il tempo per ricercare…
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