Eva Shea wondered about her daughter. Mimi went to preschool like most children, and seemed otherwise healthy. She had, however, a peculiar, chronic cough. It sounded as though Mimi smoked…
Doctors told Samantha Youakim she had hepatocellular carcinoma when she was 10 years old. As a result of this rare form of liver cancer, the experts told her she’d only…
A new clinical study shows how the internet may provide opportunities for therapy. The study’s results detail how an online program called Elevida reduces fatigue in patients with multiple sclerosis.…
Residents think of the Central Florida healthcare system as predictable. It maintains a conservative approach to practices. That was until recently, when the industry invited local video game developers to…
Reviva Pharmaceuticals Inc. (Reviva) announced on April 10th that it received Orphan Drug Designation from the United States Food and Drug Administration (FDA) for one of its experimental candidates. The…
10-year-old Shayleigh Davidson visited her sister in the hospital a lot during the last five years. Her sister, Anai, is five years old, diagnosed with spina bifida and hydrocephalus. Spending…
A young woman in Cambridgeshire received a trailblazing double lung transplant. Now she’s started a Kickstarter campaign to publish a book to help other people in similar situations, their friends…
In an $8.7 billion agreement, Swiss drugmaker Novartis recently acquired AveXis. The company moved in such a way in order to acquire a developmental therapy for spinal muscular atrophy. The…
Eva-Rose Sturgess is eighteen months old. She faces a disease for which there is no known cure: leukodystrophy. Her parents felt like their world came apart at the seams when…
A Michigan based initiative called “Let MI Doctors Decide” is picking up steam with many major healthcare organizations. As support continues to grow, “Let MI Doctors Decide” seeks to improve…
Collaboration often leads to greater success. Two advocacy groups, the Hereditary Neuropathy Foundation and True Reply have done just that to benefit patients with Charcot-Marie-Tooth disease. Their combined efforts focus…
A potential Zika treatment exists as a result of drug repurposing. The drug originally treated Hepatitis C. A new study highlights its potency against the microcephaly-causing Zika virus. Keep reading…
A proposal by California governor Jerry Brown set its sight on the Discount Drug Program for Medi-Cal patients. A group of healthcare providers, including the Orthopaedic Institute for Children came…
Within the last two decades, a type of medicine known as a biologic became popular for the treatment of autoimmune disease such as lupus, or ankylosing spondylitis. The treatments work…
Tyler Perry’s Madea may have saved Boone Begner’s life. Born with heterotaxy syndrome, Boone’s heart works with only three chambers instead of four. The condition often becomes extremely dangerous to…
Recent news from Apple shows a new series of emojis coming with the next iOS update. The set intends to “better represent individuals with disabilities.” To accomplish this, Apple partnered…
In some cases of multiple sclerosis, patients report a decrease in their sense of smell. This by itself is not unusual given the nature of the disease. A small study…
Major pharmaceutical company Pfizer recently announced the success of a new experimental product. The drug targets a disease called transthyretin cardiomyopathy, related to amyloidosis, a rare and dangerous disease that affects…
Living with a rare disease provides enough challenges on its own. For residents of Chicago, however, challenges grew even more difficult as pharmacies shut down one after another. Certain areas…
The United States Food and drug Administration recently announced its decision to grant a priority review. The privilege of expedited process, according to a press release, falls to AstraZeneca and…
Discussion on Right to Try legislation continues, and the federal government could soon change existing rules. Many people wonder whether or not patients should have the right to try potentially…
Cindy Rogers never gets a day off. She barely recalls a time when she slept for more than a handful of consecutive hours. This is because Cindy serves as primary…
Ashley Moore survived cancer. For many people, that’s enough. Moore, however, chose to give back in a surprisingly direct and immediate way. She decided to become a nurse. Keep reading…
La Jolla Pharmaceutical recently announced a new clinical trial targeting thalassemia. The trial, described as pivotal, investigates a drug referred to as LJPC-401. The treatment is intended to help patients…
A recently published study examines the response of motor nerve cells to motor neuron disease. Researchers hope that by more completely understanding this cellular response that they may be able…
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