A recent article in The American Journal of Managed Care (AJMC) heralds the approval of a third CAR T-cell therapy, called Tecartus. Kite Pharma’s cell-based gene therapy is the first…
Metformin is a popular drug used by type 2 diabetes patients. According to recent interviews conducted by reporters for Medical Xpress, a team of researchers conducted parallel rodent and…
According to a story from the CureDuchenne Blog, Dr. Kevin Flanigan of Nationwide Children's Hospital has recently dosed two Duchenne muscular dystrophy patients with an experimental gene therapy. This gene…
Currently, over 200 different mutations are linked to the development of best vitelliform macular degeneration (BVMD, or Best disease). But while certain treatments may treat certain mutations, there has…
Many people use art, music, or writing to cope with events in their life. Personally, my platform is poetry; I love the way that I can use words to…
Dr. Lindsay Wilde, an oncologist at the Hematologic Malignancies Division of Jefferson University, recently contributed to an article in the Oncology Times outlining her research team’s new study and…
By Lauren Thayer from In The Cloud Copy Sickle cell disease (SCD) is group of inherited red blood cell disorders. In a typical, healthy red blood cell, the cell is…
By Caitlin Seida from In The Cloud Copy Researchers in Russia completed a study measuring certain biomarkers among those with alcohol use disorder (AUD) and depression. The study sought to…
According to a story from mlive.com, the state of Michigan has confirmed its first case of acute flaccid myelitis, a rare disease that tends to affect children, this year. There…
In 1986, Judy and Larry Pichon were married. The couple lived a happy life in Louisiana, though their days were sometimes complicated by Judy's health. She had granulomatosis with…
Researchers discovered surprising results after performing new studies of chronic fatigue syndrome (ME/CFS) and fibromyalgia (FM). According to a report by Cort Johnson in HealthRising, the new studies give…
Rare Pediatric Disease Designation has just been granted by the FDA for an investigative therapy for lymphatic malformations (LMs). This therapy is called TARA-002 and was developed by Protara Therapeutics.…
In a recent webinar hosted by the National Organization for Rare Disorders (NORD), a number of speakers discussed an up and coming project spearheaded by the organization: the Rare Disease…
In a recent press release, biopharmaceutical company Fortress Biotech announced that their study regarding ATP7A targeted next generation DNA sequencing for Menkes disease was published in Molecular Genetics and Metabolism…
By Lauren Thayer from In The Cloud Copy COVID-19 has brought life to a screeching halt for everyone across the world. Schools cancelled, work transitioned to remote, all activities cancelled,…
Dr. Ananya Malhotra speaks to News-Medical about her research into how pancreatic cancer prognosis could be improved by using artificial intelligence. Read the source article at Health News and Information
Happy Friday! July is almost over, which means that Juvenile Idiopathic Arthritis Awareness Month is drawing to a close. But it's not too late to bring attention to this often…
By Danielle Bradshaw from In The Cloud Copy The chances of your child having Jordan’s syndrome are incredibly small. That, however, was not the reality for Joe Lang and his…
According to Parkinson's News Today, the FDA recently approved an iOS app to assist patients with neurological disorders. Developed by Abbott, the Patient Controller App offers unique telemedicine at…
Three people with an eye on the future talk about their innermost feelings and the fact that their lives may be interrupted at any time by their chronic illness.…
A recent article in BioSpace reported that Blueprint Medicines Corp. has submitted a New Drug Application (NDA) to the FDA for the investigational drug pralsetinib with an action date…
According to data from the STOMP trial involving thirty-four patients, a triple regimen has been proven to induce durable responses in pretreated patients with relapsed/refractory multiple myeloma. A recent…
Gaucher Disease Awareness Month takes place every October, but amidst this new global pandemic, planning has taken place early to figure out how to make the month as successful as…
According to a story from Youth Today, the Americans with Disabilities Act (ADA) was first passed 30 years ago, in 1990. This historic law helps protect people that live with…
Chemotherapy-induced peripheral neuropathy, or CIPN, is a common side effect of chemotherapy. A recent study aimed to uncover whether or not oxaliplatin chemotherapy increased risk of CIPN for those with…
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