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CGTx Therapies: Operational Inefficiencies and High Costs Hinder Clinical Trials

CGTx Therapies: Operational Inefficiencies and High Costs Hinder Clinical Trials

  • Post author:Patient Worthy Contributor
  • Post published:August 9, 2024
  • Post category:Rare Disease

By: Harsha K Rajasimha, Ph.D., Founder and CEO of Jeeva Clinical Trials Challenges Unique to Cell and Gene Therapies (CGTx) Clinical Trials Cell and gene therapies (CGTx) have emerged as…

Continue Reading CGTx Therapies: Operational Inefficiencies and High Costs Hinder Clinical Trials
Editor’s Choice: Tired? There’s Reason for Hope

Editor’s Choice: Tired? There’s Reason for Hope

  • Post author:Patient Worthy Contributor
  • Post published:September 2, 2016
  • Post category:Ankylosing Spondylitis/Bronchopulmonary Dysplasia/Dystonia/Narcolepsy/Rare Disease

Happy Labor Day Weekend Patient Worthians! We hope you can spend this weekend's extra time with friends and family while gearing up for fall! This week we have a post…

Continue Reading Editor’s Choice: Tired? There’s Reason for Hope
Aplastic Anemia? What To Do If You Are Rejected for Life-Saving Clinical Trial
Source: pixabay.com

Aplastic Anemia? What To Do If You Are Rejected for Life-Saving Clinical Trial

  • Post author:Alisha Stone
  • Post published:March 28, 2016
  • Post category:Aplastic anemia/Rare Disease

Recently I read an interesting article about a new med that’s been shown to speed the production of blood platelets by as much as 40% which could potentially improve the…

Continue Reading Aplastic Anemia? What To Do If You Are Rejected for Life-Saving Clinical Trial
You Want to Put What in Me? New Treatment for XSCID

You Want to Put What in Me? New Treatment for XSCID

  • Post author:James Ernest Cassady
  • Post published:March 16, 2016
  • Post category:CGD/Primary Immunodeficiencies/Rare Disease/SCID/Timely

I have two sisters, each with the remarkable talent to walk into a thrift store with only a few bucks and walk out with a brand new wardrobe. Growing up in…

Continue Reading You Want to Put What in Me? New Treatment for XSCID
Can Statins Save Your Life? Find Out Here

Can Statins Save Your Life? Find Out Here

  • Post author:Lady Kehveen Abernathy
  • Post published:December 30, 2015
  • Post category:Duchenne Muscular Dystrophy/Rare Disease

Duchenne muscular dystrophy (DMD) may not sound so bad, but it is. What's so fatal about muscle degeneration? you might ask. Well, the heart is a muscle, so there's that. Luckily,…

Continue Reading Can Statins Save Your Life? Find Out Here
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