Health Canada has recently granted market authorization to Hoffman La-Roche Limited for their neuromyelitis optica spectrum disorder treatment, ENSPRYNG. Canada is the first country to offer this medication, and hopefully…
Praise Aki Amedal, a Nigerian living in the city of Oriade, has just completed his first book entitled The Biological Prisoner . . . Finding Hope in a Failing Body.…
by Lauren Taylor from In The Cloud Copy Nearly all babies born in the United States today are tested for a certain panel of genetic disorders within 48 hours of…
by Lauren Taylor from In The Cloud Copy Long QT syndrome, also called LQTS for short, is a disorder of the heart’s rhythm that can possibly cause the heart to…
Dayton Abbott is like many kindergarteners; she loves to tell jokes, play games, and hang out with friends during recess. But her playground at Alexander Elementary School wasn't built for…
This month is Charcot-Marie-Tooth (CMT) Awareness Month. Due to COVID-19, there cannot be any of the typical events, but that doesn't mean there's nothing you can do. From a virtual…
According to BioSpace, a Phase III trial of Farxiga has produced very positive results. This chronic kidney disease (CKD) treatment was able to dramatically prolong survival in those with stages…
by Lauren Taylor from In The Cloud Copy Autoimmune uveitis is a condition in which abnormal activation of the immune cells takes place within the eye, ultimately leading to the…
by Lauren Taylor from In The Cloud Copy Having a child, especially for the first time, comes with so many unknowns and questions. What stroller to buy, what to name…
Recently, biopharmaceutical company Fortress Biotech announced positive clinical results for CUTX-101 (copper histidinate). The data highlights the efficacy of CUTX-101 for patients with Menkes disease. As there are currently no…
By Lauren Taylor from In The Cloud Copy COVID-19 has flooded headlines daily since it first reared its head in late 2019 and early 2020. Some parts of the world…
Dealing with grief is different for everybody. Unfortunately, living with a rare disease can bring sadness and grief into one's life. That is why the Livestrong Foundation has offered a…
Ariella Pacheco of Encinitas, California is a 17-year-old in her senior year at a Carmel Valley Catholic School. Ariella spoke to a reporter for MSN about her new-found passion to…
As reported in the Global News; what if you had a draining rare disease, and a life-changing treatment was out there but wasn't available in your country? At Dalhousie University…
XPhyto Therapeutics has been developing a skin patch as a delivery system to treat Parkinson's disease. They just released an update, stating that the "formula was locked," and the process…
According to an article in Newswire, medical professionals from the UK have discovered a number of protein structures that are associated with Parkinson's disease. The hope is that further research…
On August 31, 2020, biopharmaceutical company Omeros Corporation announced that it will soon move forward with clinical trials for OMS906. This decision follows clearance of an Investigational New Drug Application…
The CMT Research Foundation has announced that September will be Charcot-Marie-Tooth (CMT) Disease Action Month. The switch from awareness to action illustrates just how much CMT patients and their families…
According to an article from Newswire, the Alzheimer's Association is awarding Elixiron Immunotherapeutics one million dollars for work on their Alzheimer's treatment, EI1071. This money will go towards a clinical…
A recent article in the Korea Biomed Review reported that the joint research effort by Seoul National Medical College and Helixmith of San Diego, California, found Helixmith’s VM507 antibody effective…
When Jacqueline City went to a concert in high school, she didn't know that her life was about to change forever. At the time, Jacqueline was 18 and living in…
New Zealand has the third highest rate of inflammatory bowel disease (IBD) in the world, but there are only two drugs that are currently being funded to treat it. As…
According to a story from The Garstang Courier, Joshua Brandwood of Lancaster, UK has begun organizing a 5K run as a fundraiser for the family of Lexi Tindale, a girl…
For patients with rare diseases and their families, life is sometimes isolating. It can be difficult to explain your condition. At the same time, it is incredibly important to find…
As reported in Stem Cells News; finding the right donor for people in need of bone marrow transplants can be very tricky. This is because finding the correct match between…
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