According to a story from Chronicle Live, a medical team from Newcastle in the UK will travel to the Kerala province in southern India to treat patients with hemophilia. The…
According to NBC Right Now, the liver disease advocacy organization called The American Liver Foundation is launching an online platform designed to pair liver disease patients to clinical trials. The website,…
A story from Charcot-Marie-Tooth News highlights the necessity for genetic testing and a physical examination prior to chemotherapy in order to prevent nerve damage in people with asymptomatic Charcot-Marie-Tooth disease…
In an twist of fate, a brand new gene therapy for the treatment of Adrenoleukodystrophy (ALD) uses one of medicine's greatest nemesis, HIV, to treat this fatal genetic brain disease-- and…
Donna Keck has multiple sclerosis (MS). She's 61-years-old and has lived a life full of health complications, reports Chicago Tribune. Nevertheless, Keck battled through these challenges and eventually founded a grounded…
According to a story from watoday.com.au, Reginald Whiu, aged 73, had been complaining about back pain and was diagnosed with degeneration of the spine by his doctor. This was at…
According to an article from Righting Injustice, a recent study suggests that TNF inhibitors may increase the risk of rare cancers in pediatric patients. The study recommends that children that…
An article from SRN News is reporting that a lot of people with familial hypercholesterolemia are going through life without getting the treatments that could help them, such as statins.…
A gene therapy for Pompe disease is the first treatment of its kind to be clinically tested, reports Duke University. Researchers at the University, working with NCATS Therapeutics for Rare…
According to a story from biopharmadive.com, the Swiss pharmaceutical company Novartis has entered a partnership with researchers from the engineering and applied sciences school at Harvard University. The team will…
A new drug being developed to treat Angelman syndrome (AS) has just been approved for ‘orphan drug’ status in the U.S., reports GlobeNewswire. The drug, called GTX-101, works by activating the…
A new study conducted at Binghamton University demonstrated that pancreatic cancer cells can be killed with a dual thermal ablation process, which is the combination of freezing and heating, reports…
La Jolla Pharmaceutical recently announced a new clinical trial targeting thalassemia. The trial, described as pivotal, investigates a drug referred to as LJPC-401. The treatment is intended to help patients…
According to a story from medicalxpress.com, a recent study suggests that cognitive deficits that can occur as side effects of targeted brain cancer drugs could be successfully reversed with therapy.…
A recent story from The Independent is touting the results of a clinical trial that tested stem cells transplants for multiple sclerosis. The transplant appears to help "reset" the patient's…
According to a story from GlobeNewswire, the biotechnology company argenx announced recently that its investigational therapy ARGX-113 was granted orphan drug status by the European Commission. This designation is based…
According to a story from mysunshinecoast.com.au, an international research team has uncovered a potential biomarker that could help develop treatments for multiple myeloma, a rare form of cancer. Currently, multiple…
According to a story from the Nottingham Post, the family members of brain cancer patients are putting their time and money towards the funding of a cutting edge MRI scanner…
A recently published study examines the response of motor nerve cells to motor neuron disease. Researchers hope that by more completely understanding this cellular response that they may be able…
According to a story from Everyday Health, The U.S. Food and Drug Administration (FDA), has recently approved a new drug for the treatment of recently diagnosed patients with Hodgkin disease.…
According to a story from GlobeNewswire, The pharmaceutical company AveXis, Inc., a company that specializes in the development of gene therapies, recently announced that its candidate AVXS-101 was awarded SAKIGAKE…
According to a story from Innovation Toronto, a recent study has helped develop methods that could be used to create cell-based, personalized immunotherapy treatments that could be used to treat…
According to a story from healio.com, scientists have developed an easy to use testing method for Barrett's esophagus, which can be a precursor to esophageal cancer. The new device combines…
Sisters Nicole and Jessica Rich, both diagnosed with Batten disease, will finally be able to receive treatment at Great Ormond Street Hospital in London. Nicole, who is six years old,…
According to a story from Business Wire, there was a time when having to use a mechanical ventilator in order to breathe meant being confined at the hospital in an…
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