Loxo Oncology has announced that the US Food and Drug Administration (FDA) has granted the drug larotrectinib Priority Review, and accepted a New Drug Application (NDA) for it. These applications…
As summer approaches, let's not take our eye off the ball on awareness efforts! June is Antiphospholipid Antibody Syndrome Awareness Month! Antiphospholipid antibody syndrome is a rare autoimmune disorder characterized by…
According to a story from The Guardian, doctors are celebrating the effectiveness of an all new, experimental immunotherapy that was able to totally eliminate a case of metastatic breast cancer…
According to a story from the Pharma Letter, the Indian government has decided to take some steps to make rare disease and orphan drugs more affordable for its citizens. The…
According to a story from PR Newswire, the U.S. Food and Drug Administration (FDA) recently approved the expansion of the indication for tofacitinib (marketed as Xeljanz), which will now include treatment…
According to a story from Renal & Urology News, a recent study investigated the origins of hyperkalemia caused by certain treatments, specifically the class of drugs known as renin-angiotensin-aldosterone system inhibitors…
June is here - and so is Myasthenia Gravis Awareness Month! What is Myasthenia Gravis you say? Myasthenia Gravis (MG) is an autoimmune neuromuscular disorder characterized by weakness and rapid fatigue of any of…
According to a story from cancer.nautil.us, some cancer researchers are beginning to look at the animal kingdom in order to find new answers for finding what it takes to beat…
To read part one of this story on cystinosis, click here. Briana and Ashley are two adult women from opposite regions in the United States. Briana lives close to her…
According to Timesunion, 10 patients in New York were diagnosed with the extremely rare eye cancer called vitreoretinal lymphoma. Since all of these diagnoses happened within four years of patients…
Researchers at the Massachusetts General Hospital Research Institute and the Georgia Institute of Technology are investigating a medication currently approved to treat a type of multiple sclerosis as a possible…
According to a story from Reuters, the Danish biotech company Genmab saw its share value drop by a quarter after Johnson & Johnson, which had partnered with the company to…
Nevaeh was born on the 3rd of September at 12:38 AM by emergency section due to the cord being wrapped round her neck, which was causing her heart rate to slow…
She wears a lacy white dress with a long, white veil. Her beautifully shaped eyebrows arc over long-lashed eyes. Her smile, illuminated by bright red lipstick, speaks of the happiness…
According to a story from the Oxford Mail, Stuart and Kira Connor were devastated when their daughter Grace, who was only three years old, suddenly passed away because of mitochondrial…
Idiopathic thromocytopenic purpura (ITP) is a rare bleeding disease that affects about 3 in 100,000 people in the US-- or, at least, that's how many people are diagnosed-- according to SELF.…
Myalgic encephalomyelitis/ chronic fatigue syndrome (ME/CFS) has been a controversial condition ever since it was first diagnosed and recognized. Some uninformed doctors still believe that the syndrome is a psychological…
A new study conducted by Centers for Disease Control and Prevention found that premature babies were more susceptible to having obstructive sleep apnea (OSA), reported RadioAllen. About 1 in 10 newborns…
Hemophilia patients in Iran are not receiving the treatment they need. Usually when cases like this make the news it is due to some form of drug shortage. According to…
Researchers have carried out a study into the genetic mechanisms involved in hereditary angioedema acute attacks. They found that two genes, called uPAR and ADM, had a particularly strong influence.…
Henry Ford West Bloomfield Hospital is all about their furry friends, AKA their beloved canines, reports Detroit News. If you aren't greeted instantly by Hope and Benson, two of the…
3D printing has officially hit the medical field and it's already making noise, reports The Jerusalem Post. Recently, 3D printing was used in Israel for orthopedic surgery and found great success.…
A new study looks at the impact of a drug to treat multiple sclerosis (MS) on children of patients who take it during pregnancy, reports News Wise. Some MS patients take…
Studies show that if your father's mother, your paternal grandmother, was diagnosed with ovarian cancer, you are at a higher risk for the disease than if your grandmother on your…
Happy June everybody! We hope everyone's ready to kick off their summer, whatever that may include. This week we have two stories from younger patients who are leveraging their own…
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