According to a recent report by CNN, the UK Health Service sent an alert to general practitioners warning of a rise in the last three weeks of children who…
Cytokine storms have been prominent in the news lately due to their role in COVID-19, but researchers have been studying their connection to Castleman disease for a long time. In…
May 15th is recognized each year as Mucopolysaccharidosis (MPS) Awareness Day. The goal of this day is to help spread awareness about this group of diseases among the general public…
The European Commission has just granted their approval to Pharming for an extended indication of RUCONEST (conestat alfa) for Hereditary Angioedema (HAE). This extension allows the therapy to be utilized for…
It's official: May is Cystic Fibrosis Awareness Month! So myself, and the Patient Worthy team, are excited to bring you some stories to help build your awareness and increase patient…
It all began with an email in 2019. Matt Might, director of the Hugh Kaul Precision Medicine Institute, shot his thoughts over to neurosurgery resident Matt Davis, whose 3-year-old son…
A recent article in Biospace reported an 83% survival rate for COVID-19 patients after two infusions of the experimental drug Ryoncil, developed by Mesoblast Ltd. The patients who were…
According to Batten Disease News, Invitae and Axovant Gene Therapies partnered up to offer free genetic testing in North America. This will focus on children who are thought to…
By Jodee Redmond from In the Cloud Copy Thermo Fisher Scientific, a world leader in the life sciences community, has announced that it has developed a new test for Gaucher…
Happy Thursday! The week is almost over! One more day to go! To get you through this final bit, we have three stories that we think demonstrate different aspects of…
As sourced from the Washington Post, COVID-19 coverage has been spreading the news: people with many disabilities are scared, and we need to take care of them. For many, the…
A New Study A new study, conducted by CLS Behring, has found that a new method of administration for Hizentra as a treatment for primary immunodeficiency (PI), could improve quality…
Minorities and Healthcare As a whole, racial minorities, particularly black and Latino people, have more health comorbidities. This is due to a wide array of factors including structural elements, socioeconomic…
A recent study examined three different follicular lymphoma (FL) patients to try to better understand how the disease presents differently for different individuals. Ultimately, this study has reiterated the importance…
Are opioids an effective and frequently-prescribed treatment for hemophilia? Actually, according to Hemophilia News Today, opioids are prescribed at a much higher rate than reported. This suggests that doctors and…
Patients who better understand their condition and the necessity of treatment are more likely to experience positive outcomes, says Hemophilia News Today. This is because increased awareness and education correlates…
A recent University of Sheffield news release explores findings which highlight a potential cause of leukodystrophies: immune cells. This group of rare childhood neurological disorders impacts the myelin sheath, the…
This week I heard from a grandfather who had been wanting to take his grandson fishing. The grandson had always been too busy and had far too many organized activities.…
Technological advancement throughout the world will ultimately lead to new ideas and strategies within the medical realm. As reported by Azo Sensors, a team of Brazilian researchers is already…
APDS Activated PI3K delta syndrome (APDS) is a form of primary immunodeficiency (PI). There are fewer than 100 reported cases of the condition. APDS has two types (1 and 2),…
The FDA has recently granted GTX-102, a treatment for Angelman syndrome, the Fast Track designation. This designation means that the review process is expedited. It is meant specifically for drugs…
With 4.15 million cases across the globe, COVID-19 is at the forefront of discussion. Knowledge about the viral pandemic continues to grow each and every day. Yet there are still…
Sean Boyle is a PhD candidate at Emory University. He just signed up to participate in a trial for a coronavirus vaccine when he doesn't know the risks. That's because…
According to a story from abc7.com, a recent case study has identified what scientists believe to be the earliest case of a pediatric COVID-19 patient presenting with symptoms of pediatric…
If you're like me, you've been refreshing the news every day trying to find more information on COVID-19. After all, life changed in March; the global pandemic and its associated…
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