Recently, the MDS Foundation announced that two TP53 gene mutations result in worse patient outcomes in myelodysplastic syndromes (MDS) and acute myeloid leukemia (AML). According to their international and multi center study,…
Dayton Abbott is like many kindergarteners; she loves to tell jokes, play games, and hang out with friends during recess. But her playground at Alexander Elementary School wasn't built for…
by Lauren Taylor from In The Cloud Copy As the world continues to watch the effects of COVID-19 sweep around the world, many worry about getting infected. A study from…
Earlier this week, the FDA approved oral azacitidine (Onureg) for patients with acute myeloid leukemia (AML). According to the ASCO Post, Onureg continuously treats adult patients who previously achieved remission.…
This month is Charcot-Marie-Tooth (CMT) Awareness Month. Due to COVID-19, there cannot be any of the typical events, but that doesn't mean there's nothing you can do. From a virtual…
by Lauren Taylor from In The Cloud Copy Rheumatoid arthritis (RA) is an autoimmune and inflammatory disease, which means that your body's healthy cells are attacked by your body’s own…
According to BioSpace, a Phase III trial of Farxiga has produced very positive results. This chronic kidney disease (CKD) treatment was able to dramatically prolong survival in those with stages…
by Lauren Taylor from In The Cloud Copy Autoimmune uveitis is a condition in which abnormal activation of the immune cells takes place within the eye, ultimately leading to the…
by Lauren Taylor from In The Cloud Copy After completing an internship at the world-renowned Cleveland Clinic, one Ohio teenager is now working on changing the world for dementia patients…
by Lauren Taylor from In The Cloud Copy Having a child, especially for the first time, comes with so many unknowns and questions. What stroller to buy, what to name…
Happy Friday! Monday, Sept. 7 is Duchenne Muscular Dystrophy Awareness Day. DMD is characterized by the inability to make the protein dystrophin in muscles and can result in heart and…
by Caitlin Seida from In The Cloud Copy Isolation as a result of COVID-19 precautions is necessary but can take its toll on your physical, mental, emotional, and spiritual well-being.…
by Danielle Bradshaw from In The Cloud Copy Elaina Pechota loves to dance. Back in 2018, however, the teen had a fall during one of her classes, and her entire…
According to Genetic Engineering & Biotechnology News, researchers recently discovered a potential therapy for patients with aggressive subtypes of medulloblastoma. There are four subtypes of this condition. The first is…
Recently, biopharmaceutical company Fortress Biotech announced positive clinical results for CUTX-101 (copper histidinate). The data highlights the efficacy of CUTX-101 for patients with Menkes disease. As there are currently no…
By Lauren Taylor from In The Cloud Copy COVID-19 has flooded headlines daily since it first reared its head in late 2019 and early 2020. Some parts of the world…
Within the last month, BrainStorm Cell Therapeutics Inc. announced the publication of pre-clinical data on the NurOwn system. NurOwn technology produces autologous, bone marrow-derived mesenchymal stem cells (MSCs) for…
As reported in OncLive, intravenously-administered rigosertib failed to meet the primary endpoint within the Phase 3 INSPIRE clinical trial. Ultimately, the trial sought to understand whether rigosertib could improve overall…
Dealing with grief is different for everybody. Unfortunately, living with a rare disease can bring sadness and grief into one's life. That is why the Livestrong Foundation has offered a…
Phase III clinical trial results of the triple therapy combination for the treatment of severe aplastic anemia (SAA) were set forth in a recent News Medical Life Sciences article.…
Ariella Pacheco of Encinitas, California is a 17-year-old in her senior year at a Carmel Valley Catholic School. Ariella spoke to a reporter for MSN about her new-found passion to…
As reported in the Global News; what if you had a draining rare disease, and a life-changing treatment was out there but wasn't available in your country? At Dalhousie University…
A study has concluded that Neupro Patches are a viable treatment option for those living with Parkinson's disease, according to a Parkinson's News Today article. The patch, which can treat…
Business Insider recently interviewed Marissa Oliver, a resident of New York City, who told us about the problems she has encountered during her recovery from COVID-19. Marissa, an arts manager,…
XPhyto Therapeutics has been developing a skin patch as a delivery system to treat Parkinson's disease. They just released an update, stating that the "formula was locked," and the process…
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