Dr. Harvey Moldofsky Harvey Moldofsky is a professor emeritus at the University of Toronto. His area of focus is SARS, and since the onset of COVID-19, he has been fully…
In a story reported in News Medical Life Sciences, researchers attempting to treat rare diseases often find themselves with a dilemma- while there aren’t many patients to test treatments on in…
Sometimes, researchers find beneficial medications during clinical trials. Other times, the therapy just falls short. According to Myasthenia Gravis News, the latter is true for Firdapse (amifampridine phosphate). The…
This past week, biopharmaceutical company Mustang Bio announced that their gene therapy candidate MB-107 received Rare Pediatric Disease Designation. The gene therapy candidate is designed to treat X-linked severe…
by Lauren Taylor from In The Cloud Copy Myasthenia gravis is a neuromuscular disorder characterized by rapid fatigue and weakness of any muscles that are under the voluntary control of…
To capture the essence of palliative care, the World Health Organization defines it as the prevention and relief of suffering associated with a life-threatening illness. An article in Parkinson’s…
Did you know that over 25 million people worldwide take antidepressants? But even with this high usage, many researchers aren't sure exactly how antidepressants like selective serotonin reuptake inhibitors…
Ross Douthat, a writer for the New York Times, was first diagnosed with Lyme disease and a Bartonella infection in 2015 from a deer tick bite. The effects have lingered…
I-Mab, a biopharmaceutical firm, has begun dosing participants in Phase Ib of their trial of plonmarlimab, a rheumatoid arthritis (RA) treatment. Developers of the medication believe that it could become…
In many cases, autoimmune disorders like myasthenia gravis are treatable. However, there are some cases of refractory (treatment resistant) myasthenia gravis that presents an unmet patient need. However, researchers…
A press release issued recently by Regeneron Pharmaceuticals heralded the acceptance of a Biologics License Application by the FDA for Priority Review of its investigational drug, evinacumab. The Priority…
Ascendis Pharma has just announced that their investigative therapy for achondroplasia called TransCon CNP has just received Orphan Drug Designation from the European Commission. This same designation has already been…
by Danielle Bradshaw from In The Cloud Copy Gastroparesis is a condition in which your stomach’s muscles aren’t able to completely move food through your stomach. Symptoms of gastroparesis include…
In an editorial piece published in the New England Journal of Medicine, Dr. Michael T. Melia, M.D., and Paul G. Auwaerter, M.D., note that up to 20% of patients with…
Zacari was born with a rare neuromuscular disorder called arthrogryposis multiplex congenita. Children with the disease are unable to straighten or bend their legs or arms. Yet, according to…
by Caitlin Seida from In The Cloud Copy Those living with autoimmune disorders like uveitis and multiple sclerosis know all too well that the cells within our bodies meant to…
by Lauren Taylor from In The Cloud Copy Rheumatoid arthritis (RA) is an autoimmune inflammatory disorder that causes inflammation to the lining of your joints while also causing damage to…
Recently, the Michael J. Fox Foundation (MJFF) awarded $1.4 million in funding for Modag, a drug developer whose solutions treat patients with neurodegenerative diseases. In fact, says Parkinson's News…
by Danielle Bradshaw from In The Cloud Copy Healthy and diseased colon cells were collected and compared to each other in a recent study to discover why inflammatory bowel disease…
by Lauren Taylor from In The Cloud Copy Pediatric pulmonary arterial hypertension is a disease in which the blood flow leaving the right side of the heart faces increased resistance…
Do you want to make a difference in patient advocacy and rare disease education? Well, here's your chance. Every year, the Dystonia Medical Research Foundation (DMRF) holds a local…
Scientists have found a cluster of genes that plays a role in the development of an autism subtype. The genes are involved in controlling brain development, as well as the…
The Vestibular Disorders Association has announced its first ever Virtual Vestibular Conference. The virtual event is scheduled from September 14-18 2020 and is being held as part of Balance Awareness…
by Danielle Bradshaw from In The Cloud Copy A study was done to figure out how people with Parkinson’s disease coped with the illness in their day to day lives,…
BioFluidica recently issued an announcement that put the spotlight on its patented technology, Liquid Scan®. The new cartridge technology is designed to replace the invasive and painful bone marrow…
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