Currently, there are few - if any - ways to treat patients with myalgic encephalomyelitis, or chronic fatigue syndrome (ME/CFS). Rather than treating the condition itself, doctors often treat symptoms…
The Hindustan Times recently published an article that again puts CRISPR at the forefront of medical news. The newest CRISPR tool was designed to identify Sars-CoV-2 and prevent the transmission…
The International Waldenstrom's Macroglobulinemia Foundation (IWMF) recently held the latest webinar in its Global Education series on July 9, 2021. This webinar was a summary of research presented at the…
Compassion [kuhm-pash-uhn] noun A feeling of deep sympathy and sorrow for another who is stricken by misfortune, accompanied by a strong desire to alleviate the suffering. Compassion Corner is…
KRYPOLIS (carfilzomib) recently received conditional approval in China for the treatment of relapsed/refractory (R/R) multiple myeloma. Licensed by BeiGene, this drug is indicated for adults with R/R multiple myeloma who…
Have you ever heard of isoflavone? Well, isoflavone is part of a class of phytoestrogens, or plant-based compounds which resemble estrogen. According to Medical XPress, research from Dr. Ashutosh Mangalam,…
Breakthrough Therapy designation is granted by the FDA as a way to accelerate drug development and review. In particular, the designation is granted to drugs or biologics for serious conditions,…
According to an article in NCBI’s Drug In Context, it took the combined services of the internal medicine, neurology, and psychiatry departments to diagnose this rare disease. Anti-NMDAR encephalitis…
On July 14, 2021, biopharmaceutical company Alkeus Pharmaceuticals, Inc. ("Alkeus") shared via press release that its therapy ALK-001 (C20-D3-vitamin A) received Breakthrough Therapy designation from the FDA for the treatment…
Spinal muscular atrophy is rare progressive muscular disease that over time, erodes a patient’s movement. Without early intervention, the condition erodes the young patients ability to breathe and even swallow.…
Medical professionals are still working to uncover the cause of Alzheimer's disease. While they believe that a combination of genetic and environmental factors paired with certain lifestyle choices leads to…
According to a story from Parkinson's News Today, a three-year study has determined that dancing to music weekly may help slow the progression of Parkinson's disease symptoms. This effect included…
Normally, B lymphocytes ("B cells") are a type of white blood cell that plays a role in immune function. In healthy individuals, B cells create antibodies to fight infections and…
Accessing treatments can be difficult, especially if one is impacted by a rare disease. In fact, only 5% of rare diseases have an FDA-approved treatment. Because of this, many patients…
In a news release from mid-July, 2021, biopharmaceutical company Strongbridge Biopharma plc ("Strongbridge") shared the publication of new post hoc analyses regarding KEVEYIS (dichlorphenamide) for patients with Primary Periodic Paralysis…
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…
Researchers at NYU Abu Dhabi (NYUAD) have discovered the code that is associated with the liver’s genome (complete set of DNA) and its ability to regenerate. According to a…
Even though a drug is sometimes developed with a certain condition in mind, it can be used to effectively treat or manage alternate conditions. For example, pembrolizumab (KEYTRUDA) is…
According to a July 13 news release, biopharmaceutical company Kedrion Biopharma ("Kedrion") recently treated its first pediatric patient within the Phase 3 KIDCARES10 clinical trial. Within the trial, Kedrion…
According to MedPage Today, the FDA sent a letter to the manufacturer of the Johnson & Johnson COVID-19 vaccine on Monday containing a warning about its link to Guillain-Barre syndrome…
According to MedPage Today, new research suggests that adult obesity could increase the risk of developing Crohn's disease. Within the study, researchers evaluated how body mass index (BMI) impacted the…
Diet and nutrition play immense roles in our health. According to the Atlanta Journal-Constitution, for example, researchers discovered an association between colorectal cancer and eating red meat. “Hasn’t that been…
Beijing, China: According to an article in a sister publication of Sixth Tone, a woman living in China who has been treated during the past fourteen years for paroxysmal nocturnal…
The CDC is currently looking into three cases of melioidosis throughout the United States, according to an article published in MSN. This rare, bacterial infection is mainly found in the…
The International Pemphigus & Pemphigoid Foundation (IPPF) has recently announced that is has partnered with the American Dental Association (ADA) for a continuing education course that will help dental professionals…
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