According to Medical XPress, researchers have discovered a new potential therapy for patients with pancreatic cancer. By changing the pH balance within cancer cells, researchers could trigger cell death. Read…
Predicting the disease progression of idiopathic pulmonary fibrosis (IPF) is extremely important, as this condition progresses differently depending on the affected individual. Knowing if one has a poor outcome while…
According to Parkinson's News, researchers have discovered that specific immune cells in the blood of patients with Parkinson's disease appear up to 10 years before motor skills are impacted. This…
According to a story from Barron's, the biotechnology company Alexion Pharmaceuticals has recently announced plans to test its drug Ultomiris as a potential treatment for COVID-19. As the scientific community…
According to a story from The Charlotte Weekly, local resident Kevin Tobin recently ran 400 laps around his house---the equivalent of a marathon---to help raise money for Dan Donoher, a…
According to the UN News, the first ever World Chagas Disease Day was celebrated on April 14, 2020 to raise awareness for Chagas Disease, a rare disease spread by…
According to Ankylosing Spondylitis News, a recent study has found that TNF inhibitors are often not effective treatments for patients with ankylosing spondylitis. Read the full study in BMC Rheumatology.…
According to a story from Hematology Advisor, the drug luspatercept (marketed as Reblozyl) recently demonstrated its ability to reduce transfusion burden in patients with beta thalassemia that depend on regular…
As noted recently in an article published by Cancer Network, the FDA has cleared CYNK-001 for use in COVID-19 patients. When the investigational new drug (IND) application is submitted to…
Due to the current COVID-19 pandemic, it is very difficult for people to visit their doctors. For some, this is not the biggest deal; they can stand to miss an…
According to an article in the Asco Post, the FDA granted accelerated approval to Merck's KEYTRUDA®, pembrolizumab, for the treatment of metastatic small cell lung cancer (SCLC). The drug targets…
On Wednesday April 22nd, 2020, the World Orphan Drug Congress held a one hour webinar that was focused on how the rare disease community could respond to the ongoing coronavirus/COVID-19…
Ionis Pharmaceuticals, in a partnership with Roche, has announced that the enrollment has been completed for the third phase of GENERATION HD1, a trial intended to study the safety and…
According to Bronchiectasis News, patients with both HIV and bronchiectasis often have a difficult time being diagnosed with the respiratory condition. After researchers examined data from 14 patients, they discovered…
A clinical trial of Lu AG06466 for the treatment of Tourette syndrome ended in failure recently, as it did not meet its primary endpoints in comparison to a placebo. While…
According to a story from Yahoo News, there's no denying that the coronavirus/COVID-19 pandemic is an unprecedented experience for millions of people around the world. However, it can be especially…
In Prohealth, Marlane Quade Cook draws on her own experience with Ehlers-Danlos syndrome to question whether the medical community has enough information and education to properly diagnose all 13 subtypes…
Fulcrum Therapeutics has recently announced that it is on track to submit an Investigational New Drug application for their medication, FTX-6058. The application will likely be filed in the second…
According to a recent article in the Harvard Gazette, researchers from Harvard announced the results of a study involving animal models that brought about immunity and lasting recovery against acute…
Seattle Genetics, Bothell, Washington recently issued an announcement through Drugs.com that the FDA approved Tukysa™ combined with capecitabine and trastuzumab for patients with metastatic HER2-positive breast cancer. The drug combination…
As reported in CCA Kids Blog, the state of the world right now leaves us with many unanswered questions that can trigger a mayhem of emotions. When reconciling something that recolors…
According to Charcot-Marie-Tooth News, a recent case study found that a variation of the SEPT9 gene could contribute to the development of Charcot-Marie-Tooth disease. Read the full findings in BMC Medical Genetics. Charcot-Marie-Tooth…
12-year-old hockey player Tyler Singletary is a great team player and master on the ice. But, as reported by CBS17, Tyler found himself up against a new opponent in 2019…
April is recognized as Fabry Disease Awareness Month by the Fabry community in the US and several other countries around the world. Advocacy groups such as the Fabry Support &…
For the last month, the world has been living through a pandemic: COVID-19. The situation is rapidly changing daily. As of April 13, there have been 1.8 million diagnosed…
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