FDA Approves a Program for Expanded Treatment Access in Niemann-Pick Disease Type C
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FDA Approves a Program for Expanded Treatment Access in Niemann-Pick Disease Type C

According to a story from ir.stockpr.com, the biotechnology company CTD Holdings, Inc., recently announced that the US Food and Drug Administration (FDA) has issued an approval for an individual Investigational…

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Eosinophilic Esophagitis Patients at High Risk of Relapse After Stopping Treatment, Study Says
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Eosinophilic Esophagitis Patients at High Risk of Relapse After Stopping Treatment, Study Says

According to a story from Healio, the results of a randomized trial suggest that patients with eosinophilic esophagitis are likely to experience rapid relapse if they stop treatment. This was…

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Infant With Juvenile Myelomonocytic Leukemia Successfully Treated With Liver Cancer Drug
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Infant With Juvenile Myelomonocytic Leukemia Successfully Treated With Liver Cancer Drug

According to a story from Science Daily, the University of California San Francisco's Benioff Children's Hospitals have successfully treated an infant with juvenile myelomonocytic leukemia. The drug used for treatment…

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FDA Approves a Combination of Drugs for Diffuse Large B-cell Lymphoma

  Diffuse large B-cell lymphoma  (DLBCL) is a common type of non-Hodgkins lymphoma. World Pharma News recently reported that the FDA approved the first chemoimmunotherapy, Polivy, for DLBCL in combination with…

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The Drug Stelara Gains Approval for Moderate to Severe Ulcerative Colitis in the EU
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The Drug Stelara Gains Approval for Moderate to Severe Ulcerative Colitis in the EU

According to a story from BioSpace, Janssen Pharmaceutical Companies recently announced that the European Commission (EC) has expanded the approved indication of the company's drug ustekinumab (marketed as Stelara). This…

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This Company Just Announced Plans to Develop a Gene Therapy for Type 2A Charcot-Marie-Tooth Disease

According to a story from BioSpace, the genetic medicines company Passage Bio recently announced plans for its sixth program for gene therapy development. The company plans to work with the…

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An Experimental Drug Could be Effective for Neuromyelitis Optica, Study Results Show

According to a story from Biotech 365, the biotechnology company Viela Bio announced the publication of critical results from a recent study that tested the company's investigational drug inebilizumab as…

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An Experimental Treatment for Pulmonary Arterial Hypertension Just Earned Orphan Drug Designation

According to a story from firstworldpharma.com, the biopharmaceutical company Acceleron Pharma, Inc., recently announced that the company's experimental product candidate sotatercept has earned Orphan Drug designation from the US Food…

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This Drug Could be a Breakthrough for Severe Familial Hypercholesterolemia, But How Much Will it Cost?
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This Drug Could be a Breakthrough for Severe Familial Hypercholesterolemia, But How Much Will it Cost?

According to a story from Forbes, a new drug developed by the company Regeneron has the potential to make a real difference for people with the homozygous form of familial…

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A “Real World” Study Suggests That The Drug Apremilast Could be Useful for Behçet’s Disease
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A “Real World” Study Suggests That The Drug Apremilast Could be Useful for Behçet’s Disease

According to a story from rheumatology.medicinematters.com, a recent Italian real-world study has provided some evidence that the drug apremilast, which is considered a phosphodiesterase-4 inhibitor, could be a useful treatment…

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The Sudden Closure of Northwestern University’s Stem Cell Therapy Clinic Raises Questions That Remain Unanswered

According to a recent article in The Scientist, Northwestern Medicine’s successful autoimmune and immunotherapy program is winding down and will be closed by the end of the year. The program,…

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Companies Reach Partnership Agreement Related to an Experimental Treatment for ATTR Amyloidosis
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Companies Reach Partnership Agreement Related to an Experimental Treatment for ATTR Amyloidosis

According to a story from BioPortfolio, Alexion Pharmaceuticals, Inc. and Eidos Therapeutics, Inc., have recently struck an agreement related to the development and marketing of an experimental treatment for hATTR…

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Making History: First Drug Approved for Scleroderma-Associated Interstitial Lung Disease
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Making History: First Drug Approved for Scleroderma-Associated Interstitial Lung Disease

According to a story from finanzen.at, the drug nintedanib (marketed as Ofev) has officially been approved by the US Food and Drug Administration (FDA) as a treatment for interstitial lung…

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Biohacking: A Small Group of Amateur Biologists Are Hoping to Market Their Knockoff of a One Million Dollar Gene Therapy

  According to a recent article in Archive Today, an international band of amateur biologists, or "biohackers" announced that they intend to eventually market a knock-off of Glybera, a one…

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