Imagine having a couple more hours until you have to get up for work, but can’t fall asleep. Or what about feeling sleepy when everyone around you is waking up?…
Huntington's disease is characterized by the progressive degeneration of nerve cells in the brain. As a result of the breakdown of these very important cells, the body and mind of a…
It's that time of year again. Families across the country are making their annual pilgrimage out to the local pumpkin patch (or Kroger) to pick up fall's fruitiest porch decoration.…
Is it possible to check into the hospital and become sicker? Absolutely. Let's say you're suffering from a chronic condition, such as multiple sclerosis, cystic fibrosis, idiopathic pulmonary fibrosis or…
Patients with hepatocellular carcinoma can look forward to the FDA accelerated approval of nivolumab (Opdivo) after prior sorafenib (Nexavar) treatment. Hepatocellular carcinoma is a common form of liver cancer that cannot be…
In late September, Food and Drug Administration designated "fast track" status to the research and development of CPP-1X/sul for adults diagnosed with Familial Adenomatous Polyposis (FAP). Overseeing the project are Cancer…
Smart cars can apply the brakes for us. Smartphones can pay bills for us. Smartwatches measure blood pressure, temperature, and heart rates, as well as the passage of time. Now,…
When three-year-old Jake Burgman was born, something was wrong. Three months into his life, the Burgman's noticed that Jake was unable to lift his own head, among other developmental delays.…
There are a lot of stupid videos on the internet. It’s amazing what can catch on and go viral. Some videos are funny and feature fur-babies being adorable. Those can…
You've probably never heard of Criciúma. It's a city in Brazil known for its lumber, tile, textiles, and coal. It's also, according to the website ResearchGate, the epicenter of an extremely…
You will not often find me in the kitchen--a place that often plays a center role in the lives of families with cystic fibrosis. I have nothing against cooking—other than…
Researchers from MIT have recently identified a new way to stop the growth of glioblastoma brain tumors, bringing renewed hope in treatment options for this rare life-threatening cancer. Glioblastoma is…
October 21, 2017 Remember this deadline if you have a alpha or beta thalassemia, or another significant form of thalassemia, and are seeking an advanced degree in the US or abroad…
The future is now. A small robot called AV1 will allow a sick boy to experience the classroom from home. When you're diagnosed with a rare disease, it's hard to…
There is a definitive group of people out there who love to hate on message boards and crowd-sourced information websites, like wikis. Their chief complaint is that anyone can put…
You’re used to seeing Santa at his workshop, at the mall, under your tree—but at an art exhibit? Well, for one Alaska teen living with cystic fibrosis (CF) that became a…
For patients, caregivers, healthcare providers, and anyone interested in learning more about liver diseases, there is a website called Focus. This website is organized by CLDF, which stands for Childhood…
When Zika arrived in Latin America a few years ago, something about it had changed. It was different, more devastating. This was very strange, considering the disease had existed for…
CLICK CLICK! For some, the mundane sound a pen clicking is simply unbearable. You could be an easily peeved person or you are probably suffering from a rare disorder known…
There's a serious, rising issue brewing over health care coverage for Phenylketonuria (PKU) and it's a steaming pile of outrage. If you haven't heard of this rare disease, here's the…
When someone you love has a rare disease, it can be devastating. But every day more information is being amassed to help combat these often deadly conditions. One of the…
Developing drugs for the myriad diseases that afflict humans is a complicated process. Of course, the chemistry behind developing said drugs is complex. However, deciding what diseases and dysfunctions to…
Facebook can be a real time suck. Especially, when you’re looking for a distraction or for an old high school flame. However, if you’re looking for an informational, inspirational Facebook…
Vertex Pharmaceuticals announced in late August that the U.S. FDA accepted applications of tezacaftor/ivacaftor for patients with cystic fibrosis (CF). Specifically, this combination treatment can be used in patients ages…
Natalie Stokes was always the curvy one in her group of friends. But when she started putting on more and more weight despite cutting down to only 1,000 calories a…
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