by Danielle Bradshaw from In The Cloud Copy Gastroparesis is a condition in which your stomach’s muscles aren’t able to completely move food through your stomach. Symptoms of gastroparesis include…
In an editorial piece published in the New England Journal of Medicine, Dr. Michael T. Melia, M.D., and Paul G. Auwaerter, M.D., note that up to 20% of patients with…
Zacari was born with a rare neuromuscular disorder called arthrogryposis multiplex congenita. Children with the disease are unable to straighten or bend their legs or arms. Yet, according to…
by Caitlin Seida from In The Cloud Copy Those living with autoimmune disorders like uveitis and multiple sclerosis know all too well that the cells within our bodies meant to…
by Lauren Taylor from In The Cloud Copy Rheumatoid arthritis (RA) is an autoimmune inflammatory disorder that causes inflammation to the lining of your joints while also causing damage to…
Recently, the Michael J. Fox Foundation (MJFF) awarded $1.4 million in funding for Modag, a drug developer whose solutions treat patients with neurodegenerative diseases. In fact, says Parkinson's News…
by Danielle Bradshaw from In The Cloud Copy Healthy and diseased colon cells were collected and compared to each other in a recent study to discover why inflammatory bowel disease…
by Lauren Taylor from In The Cloud Copy Pediatric pulmonary arterial hypertension is a disease in which the blood flow leaving the right side of the heart faces increased resistance…
Do you want to make a difference in patient advocacy and rare disease education? Well, here's your chance. Every year, the Dystonia Medical Research Foundation (DMRF) holds a local…
Scientists have found a cluster of genes that plays a role in the development of an autism subtype. The genes are involved in controlling brain development, as well as the…
The Vestibular Disorders Association has announced its first ever Virtual Vestibular Conference. The virtual event is scheduled from September 14-18 2020 and is being held as part of Balance Awareness…
by Danielle Bradshaw from In The Cloud Copy A study was done to figure out how people with Parkinson’s disease coped with the illness in their day to day lives,…
BioFluidica recently issued an announcement that put the spotlight on its patented technology, Liquid Scan®. The new cartridge technology is designed to replace the invasive and painful bone marrow…
According to a recent article in Medscape News, myocardial infarction (coronary artery blockage) and cerebrovascular incidents (stroke) have a direct correlation to diabetic retinopathy. The risk doubles when the…
As reported in Parkinson's News Today, three research teams are set to dig deeper into developing a potential diagnostic tool to diagnose Parkinson’s- an opportunity awarded in the form of…
According to BioSpace, the first patient has been enrolled in a trial of pamrevlumab, a Duchenne muscular dystrophy treatment. The third phase of LELANTOS plans to evaluate the drug's effects…
Arrowhead Pharmaceuticals has began dosing patients in its AROENaC1001 trial, which evaluates ARO-ENaC as a treatment for cystic fibrosis. 54 patients will be treated with this therapy in an effort…
This week, Regeneron Pharmaceuticals announced that their Biologics License Application (BLA) for evanicumab, a treatment for homozygous familial hypercholesterolemia (HoFH), was granted Priority Review status by the FDA. The…
According to a story from curetoday.com, patients living with mantle cell lymphoma, a rare form of blood cancer that makes up only around six percent of diagnosed non-Hodgkin lymphoma cases…
Corbus Pharmaceuticals has just announced that participant enrollment for their Phase 3 trial of lenabasum for dermatomyositis has been completed. Dermatomyositis Dermatomyositis (DM) is a rare autoimmune disease. It can…
by Danielle Bradshaw from In The Cloud Copy Information provided by the Michael J. Fox Foundation showed that the majority of patients that had Parkinson’s disease and also contracted COVID-19…
According to a recent article in Medscape News, myocardial infarction (coronary artery blockage) and cerebrovascular incidents (stroke) have a direct correlation to diabetic retinopathy. The risk doubles when the…
The Cystinosis Research Network (CRN) has created a new program to bring light to cystinosis families during these uncertain times. It is called the Brighter Days Care Package Program. Brighter…
Would you be shocked to find out that before Evrysdi, there were zero orally-administered drugs approved to treat patients with spinal muscular atrophy (SMA)? But now, things have changed. Last week,…
Nobody knows the exact cause of Parkinson's disease. However, many researchers believe that environmental triggers may play a factor. Now, the Michael J. Fox Foundation (MJFF) is encouraging American…
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