According to a story from CureDuchenne, the biotechnology company Dyne Therapeutics recently announced that CureDuchenne Ventures has made an equity investment that will support the development of all new precision…
When some people hear "placebo effect," it conjures up images of sugar pills designed to stimulate patient belief. But according to Healio, the term has a different meaning in…
Emily Knakmuhs's two-and-a-half-year-old Kennedie had just made it past a tough couple of years. When she was born, her family noticed she wasn't growing, but her pediatrician attributed it to…
As originally reported in News Medical, a new study suggests that gastric bypass bariatric surgery may be the most effective treatment for non-alcoholic fatty liver disease (NAFLD). This disorder currently…
On March 24th, 2020, Patient Worthy released a story announcing the formation of a Coronavirus Emergency fund by the American Kidney Fund (AKF). The goal of this fund is to…
According to a press release from the Boston Children's Hospital, a study has discovered the efficacy of CRISPR-Cas9 gene-editing technology in the treatment of facioscapulohumeral muscular dystrophy (FSHD). As…
According to a story from Fierce Biotech, there have been some impressive advances in the treatment of cystic fibrosis recently. The latest milestone was in developing and approving the drug…
According to a press release on Global Newswire, Novartis has received a positive opinion on Cosentyx® from the Committee for Medicinal Products for Human Use (CHMP). This positive opinion…
Research findings can sometimes come from unexpected places. For example, according to Parkinson's News Today, the benefits and shortcomings of an investigative gene therapy were explored through the post-mortem analysis…
People across the globe are experiencing an unprecedented time of uncertainty as COVID-19 continues to spread. However, this pandemic has also brought about something wonderful: people stepping up to…
Hi everyone, We hope you're having a peaceful quarantine and taking care of yourself. As we all know, updates about COVID-19 is dominating the news right now. Of course, infomation…
As stated in a press release from the University of Illinois at Urbana-Champaign, researchers have discovered a bacterial protein fragment that is destructive to lung tissue. This can rapidly…
According to a press release from FirstWord Pharma, Gen and Alnylam Pharmaceuticals have signed an exclusive distribution deal in Turkey for RNAi therapeutic ONPATTRO. This therapy drug will treat…
According to a story from hepmag.com, a panel of experts is recommending a name change for non-alcoholic fatty liver disease (NAFLD) and is instead proposing that the condition be called…
Want to learn more about recognizing symptoms and diagnosing patients? Well, now you can. In a MedPage article, authors encourage readers to follow along on a case study to…
Cystic fibrosis is caused by a mutation in the gene CFTR. This gene involves a protein that affects the chloride on cells; without this chloride the surface of the…
According to a story from pharmaphorum.com, Jim Kuhn had a successful career in business for over 30 years, but everything changed a decade ago when he was first diagnosed with…
"A steak saved my life," writes columnist Damon Young, 41, in his article for GQ, as he shares the story of his diagnosis with Takayasu's arteritis. After over-indulging at dinner,…
In a period of unprecedented changes, it is understandable that people may question what their lives may look like moving forward. COVID-19 has now spread to 196 countries and…
As originally reported in Fabry Disease News, the potentially fatal genetic disorder Fabry disease can be diagnosed most effectively in infancy by newborn screening programs. By identifying the disease early,…
As originally reported in Smart Parenting; many families with rare diseases are struggling to keep up with their healthcare regime as new restrictions block families from accessing doctors and normal…
In a Special Issue of the journal Disease Models and Mechanisms Highlights, James J. Dowling et al describes pediatric neuromuscular diseases as mostly genetic and affecting areas of the peripheral…
Pam Kelley, a reporter whose focus is on the challenges facing people below the poverty level, submitted this story to the Charlotte Magazine. Pam conducted interviews with Cheryl Potts over…
According to a story from Pulmonary Hypertension News, the results of a recent phase 3 clinical trial have determined that patients with connective tissue disease-associated pulmonary arterial hypertension (CTD-PAH) stand…
As originally reported in Global News.,New Brunswick teen Mackenzie Walsh will be 16 this week, but she doesn't want a car or a sweet 16 party. She wants to go…
© Copyright 2024 Patient Worthy
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
