Eureka Alert recently published a statement by a team of researchers that early results of a new method of treating Alzheimer’s have been “absolutely spectacular.” The new antibody-based therapy…
What does it mean to you to be living with a rare disease or chronic illness at this time of year? Over the years, since I was diagnosed I've never…
24-year-old Georgia Hughes was concerned when she noticed that her son Myles, age 3, had missing teeth. After a number of doctor visits and MRIs, Myles was diagnosed with 4H…
The Tokyo University of Science recently published a report stating that its team of scientists was successful in developing a polymer-based-hydrogel, a welcomed improvement to the complicated formulations currently in…
According to Charcot-Marie-Tooth News, researchers have associated HINT1 gene mutations with neuropathy in Greek patients with Charcot-Marie-Tooth disease (CMT). In the past, HINT1 was linked to CMT in central and southeastern Europe. However, researchers…
A lack of patient engagement is an issue across many rare diseases, with atypical hemolytic uremic syndrome (aHUS) acting as the perfect example. In fact, aHUS patient organizations are still…
According to a recent article from Pharmacy Times, Octapharma’s cutaquig has been approved by the FDA to treat patients who are 2 years of age or older with primary humoral…
Look out, Nebraska - there may soon be an uptick (see what we did there?) of Lyme disease cases within your state. Just about two years ago, Borrelia burgdorferi (B. burgdorferi),…
Written by Lucy Scott The 9th of October 2014 would be a day I would never forget... but in actuality, I don’t remember that day nor the years before. Every…
Geraldine is Senior Vice President of TheGrio’s, known as Black America’s News. Although she never met Virgil Abloh, she followed his career and knew of his many talents. Geraldine says…
In 1960, the FDA approved chlorthalidone for hypertension (high blood pressure). However, doctors were unsure whether this therapy could benefit patients with advanced chronic kidney disease (CKD) who had high…
The vaccines for COVID-19 have allowed us to return to normalcy - partially, at least. Now, a UCLA study has discovered that there may be a way to curate a…
A recent article in the Northern Kentucky Tribune highlights a rare condition that has been exposed by new technology. Cardiologists have found that many patients diagnosed with heart failure are…
Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we think is of particular interest…
According to an article from the National Hemophilia Foundation, CSL Behring and uniQure have recently provided an update on their phase III HOPE-B trial. This study is evaluating etranacogene dezaparvovec,…
Currently, the standards-of-care for patients with Hurler syndrome, or one of the forms of mucopolysacchardiosis type I (MPS I), include enzyme replacement therapy and hematopoietic stem cell transplants. However, Medical…
It is no secret that medical research can provide crucial insights into disease pathology, prognostic factors, and patient outcomes. Recently, a research team from Hokkaido University in Sapporo, Japan dove…
In early December 2021, specialty pharmaceutical company Aytu BioPharma, Inc. ("Aytu") announced that its therapy AR101 (enzastaurin) earned Orphan Drug designation from the FDA. According to the announcement, the therapy…
According to an article from MedPage Today, Waldenström's macroglobulinemia (WM) is a rare form of lymphoma. Only about 1,500 cases are diagnosed each year in the US. In this story,…
Studies show that there is a relationship between illness or death (morbidity or mortality), scleroderma renal crisis (SRC), and a person’s race. A study using data from the U.S. Military…
Intercept has withdrawn its application for obeticholic acid (OCA) as a treatment for nonalcoholic steatohepatitis (NASH) in Europe. This decision comes after the FDA rejected the company's application in the…
Dr. Yi Xiao, oncology instructor at MD Anderson Cancer Center, and his associates discovered a unique role for antihistamines while searching for factors that may influence responses to immunotherapy. As…
Targeted Oncology recently published a report citing a promising class of drugs to treat recurrent platinum-resistant ovarian cancer (PROC), often associated with a poor prognosis. PROC eventually occurs to a…
Allegra Sturdevant, age 21, averages thousands of views on her TikTok videos, many of which describe her experiences with Marfan syndrome. According to an article in The Daily Universe, the…
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…
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