Rare diseases sufferers are the unsung heroes who often fall into the shadows behind more common cancers, but some scripted and reality shows are casting a spotlight on them. In…
Nanette Whitfield, stood beside her best friend and husband as amyotrophic lateral sclerosis (ALS) painfully took his life, reported The Record Courier. Watching someone you love slowly lose everything has…
It's hard to find funding for rare diseases research. Patients and the people who love them don't have the same established networks of support that help people struggling with more…
When someone is diagnosed with a rare disease and it looks like their days could be numbered, it can often be difficult to cope. Many people simply don't want to…
According to an article at publicnow.com, the FDA has granted Breakthrough Therapy Designation to avelumab combined with INLYTA (axitinib) for people with advanced renal cell carcinoma. This designation should accelerate…
Good news for Prometic Life Science new drug application! The pharmaceutical company has been searching for a cure for idiopathic pulmonary fibrosis (IPF), a rare lung disease which you can…
According to a story from wect.com, Dr. Jorge Figueroa, who has been a teaching for nine years at the University of North Carolina at Wilmington, has developed a reputation as…
For Johanna Watkins, a woman from Minnesota, life can be like walking through a minefield. Ms. Watkins had mast cell activation syndrome. As a result, exposure to everyday experiences such…
The Chinese Zhiying family face their ultimate breaking point when they learn they can no longer afford the medical bills needed to save their 7-month-old son, Yiwei, who is fighting…
Despite the obvious cliché nature of the old adage, knowledge really is power. Technology and medical advancements give doctors and researchers more information than anyone could have fathomed even a…
Doctors always emphasize the importance of sleep for newborn babies, but some babies may have greater challenges to face when it comes to getting a solid night of sleep. A…
Doctors told Shawn Rogers, who they had diagnosed with Pelizaeus-Merzbacher disease, that he might only have days to live. However, today he is swimming with dolphins, a dream that he…
A new study suggests that the antidepressant medication clomipramine may function to relieve symptoms of multiple sclerosis. In this instance, the drug was tested to treat progressive multiple sclerosis, in…
Skylar Marie came into the world as a beautiful healthy baby. It wasn't until 2 months later that her and her family's world would change forever. She was diagnosed with…
Olivia Ports recently performed for over a thousand people, including the Mayor and Governor of Chicago, helping to raise $3.75 million for research by Lurie Children’s Hospital in only one…
One of the medical research field's biggest developments recently - within the last 5 years! - is a new form of gene editing, also know as genome editing. Gene editing refers to…
Around 15,000 people are to receive free eye treatment thanks to the efforts of Senator Mustafa Bukar. The senator represents the Katsina North Senatorial Zone. Senator Bukar announced the event…
Drug research is taking a plunge to the underwater abyss. The nation's opioid crisis has been declared a national public health emergency. Along with the Department of Defense, the University…
Good news for patients who suffer from ankylosing spondylitis (AS). There may soon be a new option for treating their disease if the results of a new trial support the…
A new study comparing two different treatments demonstrates that both could be effective in treating hydrocephalus. This condition is characterized by a buildup of cerebrospinal fluid inside the brain. In…
Happy New Years, Patient Worthians! New year, new you... new treatment news? This week, we have an article about a molecule that could change the way we treat cystic fibrosis.…
The more scientists learn about gut bacteria, the more fascinating it becomes. It can affect your mood, the foods you crave, and according two new studies, it can even change…
While April Archote faces the physical pain and financial hardships of living with a rare brain disease, she continues to be positive and count her blessings, CCHeadliner reported. In 2013, April was…
A new study from researchers at UCSF found that a simple tool could optimize kidney treatment in children, by reducing dialysis and increasing pre-emptive kidney transplants. The tool is called…
There rare disease world has another rising hope in research and development. Her name is Christina Waters, and she is the founder and CEO of Rare Science, a California non-profit…
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