Teen with vWD Joins Cast of “Hemophilia: The Musical”
Many people use art, music, or writing to cope with events in their life. Personally, my platform is poetry; I love the way that I can use words to…
Many people use art, music, or writing to cope with events in their life. Personally, my platform is poetry; I love the way that I can use words to…
Dr. Lindsay Wilde, an oncologist at the Hematologic Malignancies Division of Jefferson University, recently contributed to an article in the Oncology Times outlining her research team’s new study and…
Last month, at the American Academy of Dermatology (AAD) Virtual Annual Meeting, Dr. Dedee F. Murrell, MD, explained the efficacy of rilzabrutinib for treating pemphigus. According to MDedge, many…
As COVID-19 continues to spread, the rush for a treatment or cure continues. Today, on August 4, there are 18.2 million diagnosed cases worldwide, with an associated 692,000 deaths.…
By Lauren Thayer from In The Cloud Copy Sickle cell disease (SCD) is group of inherited red blood cell disorders. In a typical, healthy red blood cell, the cell is…
By Caitlin Seida from In The Cloud Copy Researchers in Russia completed a study measuring certain biomarkers among those with alcohol use disorder (AUD) and depression. The study sought to…
Chronic pain affects about two-thirds of those with Parkinson's, making it the major non-motor symptom of the disease. A study published in Movements Disorders has found that anandamide and glucocerebroside…
What causes developmental disorders? How can the human genome play a role in diagnosing and treating these conditions? Well, a team of scientists from the Salk Institute recently set…
According to a story from mlive.com, the state of Michigan has confirmed its first case of acute flaccid myelitis, a rare disease that tends to affect children, this year. There…
INO-3107, a treatment for recurrent respiratory papillomatosis (RRP), has recently received the Orphan Drug Designation from the FDA. This treatment is currently being evaluate in a Phase 1/2 trial by…
In 1986, Judy and Larry Pichon were married. The couple lived a happy life in Louisiana, though their days were sometimes complicated by Judy's health. She had granulomatosis with…
Researchers discovered surprising results after performing new studies of chronic fatigue syndrome (ME/CFS) and fibromyalgia (FM). According to a report by Cort Johnson in HealthRising, the new studies give…
Rare Pediatric Disease Designation has just been granted by the FDA for an investigative therapy for lymphatic malformations (LMs). This therapy is called TARA-002 and was developed by Protara Therapeutics.…
An investigative therapy for hemolytic disease of the fetus and newborn (HDFN) has just received the FDA's Rare Pediatric Disease and Orphan Drug Designations. This therapy is called nipocalimab and…
In a recent webinar hosted by the National Organization for Rare Disorders (NORD), a number of speakers discussed an up and coming project spearheaded by the organization: the Rare Disease…
By Danielle Bradshaw from In The Cloud Copy Shimmer Research has announced that OWEAR - the Open Wearables Initiative - has decided to make their health technologies, like their database…
Moebius Syndrome Moebius syndrome is a rare condition that causes an inability to move the eyes laterally and facial paralysis. A similar type of paralysis can also occur as a…
Fast Track Designation and Rare Pediatric Disease Designation have just been awarded from the FDA to HemoShear Therapeutics. This designation was given to their new investigative therapy for propionic acidemia…
COVID-19 can't stop the American Society of Retina Specialists (ASRS)! Although their meeting needed to be held online this year thanks to the viral pandemic, the ASRS recently ran…
In a recent press release, biopharmaceutical company Fortress Biotech announced that their study regarding ATP7A targeted next generation DNA sequencing for Menkes disease was published in Molecular Genetics and Metabolism…
By Lauren Thayer from In The Cloud Copy COVID-19 has brought life to a screeching halt for everyone across the world. Schools cancelled, work transitioned to remote, all activities cancelled,…
According to a story from PR Newswire, the biotechnology company INOVIO has just announced that the company's investigational product candidate INO-3107 has earned Orphan Drug designation from the US Food…
Dr. Ananya Malhotra speaks to News-Medical about her research into how pancreatic cancer prognosis could be improved by using artificial intelligence. Read the source article at Health News and Information
According to GlobeNewswire, BridgeBio Pharmaceuticals and the Ivy Brain Tumor Center have recently began their Phase 0/2 trial of infigratinib. This treatment is meant for those with recurrent glioblastoma that…
As reported in Medical Xpress, researchers are studying how patients using bisphosophonates as part of a treatment regime to avoid fractures associated from osteoporosis are affected by "drug holidays" when…