It's hard to believe it's already been about a month since the hemophilia A community received this exciting news! In case you missed it, there's a new drug that got…
Genetic engineering has, for a long time, been a highly heated and contested issue. One must weigh the ethical ramifications and risks of engineering human embryos with the huge potential…
While multiple myeloma treatment has made significant advances in recent years, the prospect of a cure remains as elusive as ever—just as it does for all cancers. But that may…
A little thing called "genomic technology" could just be a game changer for people who suffer from idiopathic pulmonary fibrosis (IPF.) What is genomic technology? Glad you asked. Genomics is…
In the mid-1990s, many in the United States were first exposed to the somewhat strange juxtaposition of choreographed leg flailing and still upper bodies. This was, of course, Riverdance. This…
We’ve all been there. In the grocery store or at the mall or at the amusement park, when a child starts to act out, much to the chagrin of the…
There’s a lot that the marginal zone lymphoma community needs, but there is also a lot being said. Results from clinical trials are coming in, and patient testimonials are shedding…
Our nation's public health centers are the unsung heroes of health care. Each year, more than 9,000 health centers around the U.S. serve over 25 million Americans, including 300,000 veterans,…
There's a lot happening in the cystic fibrosis world, so here's the latest scoop. Cystic fibrosis (CF) is a genetic disease that causes progressive and constant lung infections as well as…
A recent study found that a specific bacteria may be the distinguishing factor between cardiac sarcoidosis and other conditions that affect the heart. This data suggests that this bacteria may…
They say, “Necessity is the mother of invention.” This maxim goes for everything from nuclear technology (the Manhattan Project was a direct result of World War II) to the Snuggie®…
There’s a lot happening in the adrenoleukodystrophy (ALD) world, so here’s the latest scoop. Adrenoleukodystrophy, or ALD for short, is a genetic rare disease that destroys the protective sheath surrounding…
In late July of this year, the results from a scientific preclinical trial were published in which a research team in Europe discovered initial signs that could pave the way…
Do you remember the "Heartbreak of Psoriasis"? Back in the '60s, some Mad Men came up with that catchy campaign to sell a "new healing discovery" that could clear up…
The U.S. FDA just granted breakthrough therapy designation to a new mantle cell lymphoma treatment called acalabrutinib! This drug is specifically for people who have already gone through at least…
Klippel-Feil Syndrome Awareness Day began five years ago, when a small group of people decided a specific day each year should be set aside, to help the KFS community speak…
As a research geek who has researched and written dozens of articles about Parkinson's disease (PD), let me assure you there is a lot of bad information out there. But there…
What do you think of when you hear the word “family?” You may consider your parents, siblings, grandparents, aunts, and uncles. No matter whom you include, we all share one…
They say that technology has made life easier, faster, more comfortable, and on and on and on. Who this “they” is, I don’t know. While technology has made certain parts…
The process of getting a treatment approved by the FDA is long and involved. Needless to say, the process is so complicated to protect us, the people who will be…
There is nothing worse than a summer cold. I should know. I am the proud owner of a bonafide summer cold complete with a runny nose, sore throat, coughing fits,…
Dogs have been helping humans for centuries. As early as the mid-1700s, dogs were being used by the blind as guides. In 1929, The Seeing Eye, the first guide dog…
Recently, the U.S. FDA has deemed a particular idiopathic pulmonary fibrosis (IPF) drug "orphan drug status" worthy. Last week, on July 25, 2017, it was reported that the FDA granted…
Let’s talk clinical trials. Clinical trials are part of clinical research and at the heart of all medical advances. Clinical trials look at new ways to prevent, detect, or treat…
Welcome Back to Editor's Choice! The end of the week is finally here, and we have some reading material for you. First, we have an awesome story of a CF…
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